Learn about the promising advance in prenatal treatment of spinal muscular atrophy, introducing a potential approach to suppress symptoms of the disorder in infants.

All biological function is dependent on how different proteins interact with each other. Protein-protein interactions ...

Why did humans start speaking? Scientists suggest genetics played a big role – and they say the evolution of this singular ...

Qure's AMT-130 shows 80% Huntington's progress reduction, eyeing FDA approval. Click here to read why I rate QURE stock a Buy ...

In their effort to answer a decades-old biological question about how the hepatitis B virus (HBV) is able to establish infection of liver cells, researchers have identified a vulnerability that opens ...

In their effort to answer a decades-old biological question about how the hepatitis B virus (HBV) is able to establish infection of liver cells, research led by Memorial Sloan Kettering Cancer Center ...

A toddler was successfully treated for a rare genetic disease, spinal muscular atrophy, after world-first in-womb therapy.

A gene called high mobility group A1 (HMGA1) may be the key that opens the door to the development of colon cancer, according ...

Cancer arises when your cells grow uncontrollably and refuse to die when they should. Normally, your body is equipped with ...

"We were delighted to discover not only important details about the mechanisms of HBV gene regulation, but also a promising ...

Scientists in Sheffield working to understand why some breast cancers come back years later and form incurable secondary tumours, have received a funding boost.

Ionis relies on upfront payments and licensing fees from partners, as well as Spinraza royalties, to drive revenue today, but its rapidly advancing portfolio should help diversify revenue. 2025 is ...