Vertex Pharma wins EU backing to expand label for Kaftrio cystic fibrosis drug
Vertex Pharmaceuticals (VRTX) stock in focus as company secures EU backing to expand label for its cystic fibrosis therapy ...
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CHMP Recommends Vertex's Kaftrio, Kalydeco Combo for Additional Cystic Fibrosis Patients
The committee supports approving the CFTR modulator for patients 2 years and older with at least one non-class I CFTR gene mutation.
Vertex Pharmaceuticals gets CHMP opinion recommending Kaftrio label expansion
Vertex Pharmaceuticals (VRTX) announced that the European Medicines Agency’s Committee for Medicinal Products for Human Use adopted an opinion ...
Pharmaceutical Technology13h
Alltrna plans to tackle rare diseases using tRNA-based therapies
Alltrna’s CEO Michelle Warner said that the approach allows for basket trials that can group patients with different diseases ...
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Vertex Severs Liver Gene Therapies Partnership with Verve
The companies were two years into a four-year, $400 million agreement aimed at developing and marketing gene therapies ...